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canavan disease/dopamini

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NakalaMajaribio ya klinikiHati miliki
1 matokeo

A next step in adeno-associated virus-mediated gene therapy for neurological diseases: regulation and targeting.

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Ingia / Ingia
Recombinant adeno-associated virus (rAAV) vectors mediating long term transgene expression are excellent gene therapy tools for chronic neurological diseases. While rAAV2 was the first serotype tested in the clinics, more efficient vectors derived from the rh10 serotype are currently being evaluated
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